| December 30, 2008 |
Families of Spinal Muscular Atrophy Funded Stem Cell Motor Neuron Replacement Program
Results and current status.
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| December 29, 2008 |
Trophos Increases Focus on Neuroprotection Including Spinal Muscular Atrophy
Read the details here.
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| December 29, 2008 |
Families of Spinal Muscular Atrophy Sponsored Clinical Trials
Summary of progress this year.
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| December 22, 2008 |
Paper Published in the Prestigious Journal Nature on Spinal Muscular Atrophy
Pluripotent Stem Cells Derived From a SMA Patient.
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| December 17, 2008 |
Spinal Muscular Atrophy Paper Published in Human Molecular Genetics on Increasing Muscle Mass in SMA
By Dr. Chris Lorson and Colleagues.
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| December 4, 2008 |
Families of Spinal Muscular Atrophy Funding of Basic Research Leads to 17 New Publications in 2008
Details can be found here.
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| December 3, 2008 |
Spinal Muscular Atrophy paper published in Journal of Pediatric Surgery
By Dr. Mary Schroth and colleagues.
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| November 6, 2008 |
TREAT-NMD Press Release
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| November 6, 2008 |
Workshop on clinical outcome measures in Spinal Muscular Atrophy
Press release on results of the meeting.
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| October 9, 2008 |
Link to Article from ACS Chemical Biology
Toward An Effective Treatment For A Major Hereditary Disease, Spinal Muscular Atrophy
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| October 8, 2008 |
Protein Linked to Spinal Muscular Atrophy Identified
Read the press release from Families of SMA here.
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| September 25, 2008 |
Multi-Center Trial in Infants with Type I Spinal Muscular Atrophy is Currently Recruiting
Click here for details and status.
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| September 3, 2008 |
Stem Cell Transplant Benefits Mice with Spinal Muscular Atrophy
Researchers at the University of Milan published a paper in the "Journal of Clinical Investigation" showing transplant of spinal cord neural stem cells into mice with Spinal Muscular Atrophy improves survival and function.
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| August 27, 2008 |
Families of Spinal Muscular Atrophy Funded Research Study Published in "Human Molecular Genetics"
Click here to read more about the paper entitled "Embryonic motor axon development in the severe Spinal Muscular Atrophy mouse", by lead author Dr. Vicki McGovern from the laboratory of Dr. Arthur Burghes at the Ohio State University.
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| August 19, 2008 |
Spinal Muscular Atrophy Symposium at the Annual Meeting of the American Society of Gene Therapy
Click here for details on the Spinal Muscular Atrophy Symposium at the meeting and the letter thanking the organizing groups.
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| August 11, 2008 |
SMA Research Results Published in Annals of Neurology
Click here to read more on the paper: "Sustained Improvement of Spinal Muscular Atrophy Mice Treated with Trichostatin A Plus Nutrition", by Dr. Charlotte Sumner at Johns Hopkins, partially funded by Families of SMA.
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| July 9, 2008 |
Multi-Center Trial of Valproic Acid and Carnitine in Infants with Type I Spinal Muscular Atrophy is Currently Recruiting at Six Centers
In April Families of SMA announced a new clinical trial designed to evaluate the combination of Valproic Acid (VPA) and L-Carnitine for the treatment of SMA in infants with Type I SMA, called Carni-Val Type I. This trial is fully funded by Families of SMA. See here for details on specific sites.
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| June 30, 2008 |
New Edition of Compass Now Online
Updates on clinical trials, including early results from the Carni-Val trial.
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| June 26, 2008 |
California Stem Cell Inc. discusses plans for SMA clinical trials at the BIO 2008 Conference
Newspaper article in the "Orange County Register" focusing on motor neuron replacement therapy for SMA, funded by Families of SMA.
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| June 16, 2008 |
Families of SMA and Paratek Pharmaceuticals Extend and Expand Drug Discovery Collaboration for Spinal Muscular Atrophy
Read the full press release here.
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| May 29, 2008 |
Special Report on Stem Cell Based Therapies Published in "Forbes"
A "Forbes" article focuses on FSMA partner California Stem Cell and the use of stem cell-derived motor neurons to treat SMA and ALS.
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| May 18, 2008 |
Latest Edition of Compass Newsletter Now Available Online
In this edition, Families of SMA announces the award of 9 new research grants.
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| April 25, 2008 |
SMA Research Published in the Journal "Science"
Brunhilde Wirth and her group from the Institute of Human Genetics, Cologne, Germany, have reported the identification of the first modifier gene able to fully protect individuals from developing SMA. The work was partly funded by Families of SMA.
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| April 10, 2008 |
SMA Research News
A summary of recent publications from our April 2008 eblast.
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| February 19, 2008 |
Stem Cell Press Release
Collaboration between FSMA; University of California, Irvine; and California Stem Cell for safety studies for stem cell therapy in SMA.
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| February 12, 2008 |
FSMA-deCODE research published in the Journal of Medicinal Chemistry
See the abstract.
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